Pharmacotherapy of Rare Diseases in Serbia: The Current State of Art

Rare diseases affect less than 1 in 2000 or 5 in 10,000 people by definition. Most of those diseases have genetic basis (80% of cases) and first symptoms appear in early childhood (50% of cases). Most of these diseases are chronic and degenerative and pharmacotherapy is not available for many of the...

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Autores principales: Brkić, Branislava Medić, Stopić, Bojan, Vujović, Katarina Savić, Divac, Nevena, Vučković, Sonja, Stojanović, Radan, Srebro, Dragana, Basailović, Miloš, Prostran, Milica
Formato: Capítulo de libro
Lenguaje:inglés
Publicado: IntechOpen 2020
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Acceso en línea:https://www.intechopen.com/chapters/71130
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