Recent Advances in Targeted Genetic Medicines for Cystic Fibrosis

The cystic fibrosis transmembrane conductance regulator (CFTR) gene was discovered just over 30 years ago, and soon after, gene therapy for cystic fibrosis (CF) has been rapidly and continually developing. Recently, novel gene therapy strategies have been developed, including mRNA delivery, genome e...

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Autores principales: Elboraie, Salsabil, Kafetzis, Konstantinos N., Shrivastava, Rajeev, Tagalakis, Aristides D.
Formato: Capítulo de libro
Lenguaje:inglés
Publicado: IntechOpen 2021
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Acceso en línea:https://www.intechopen.com/chapters/72305
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