Advances in Cellular and Cell-Free Therapy Medicinal Products for Huntington Disease Treatment

Huntington’s disease (HD) is a neurodegenerative disorder caused by the expansion of CAG repeats in the huntingtin gene. The disease causes the progressive degeneration of neurons affecting particularly the medium spiny neurons (MSNs) within the striatum. The mHtt inclusions promote neurodegeneratio...

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Autores principales: Kerkis, Irina, Araldi, Rodrigo Pinheiro, Wenceslau, Cristiane Valverde, Mendes, Thais Biude
Formato: Capítulo de libro
Lenguaje:inglés
Publicado: IntechOpen 2022
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Acceso en línea:https://www.intechopen.com/chapters/80659
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