Perspective Chapter: Emerging Innovations in Gene Therapy for Sickle Cell Disease and Beta-Thalassemia
<p id="p1">Hemoglobinopathies such as sickle cell disease (SCD) and beta (β)-thalassemia are inherited disorders characterized by defective or insufficient β-globin chain production, resulting in chronic anemia, multi-organ damage, and reduced life expectancy. Affecting millions worldwide,...
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| Main Authors: | , , , , , , , , , |
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| Format: | Book Chapter |
| Language: | English |
| Published: |
IntechOpen
2025
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| Subjects: | |
| Online Access: | https://www.intechopen.com/chapters/1226682 |
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