Perspective Chapter: Emerging Innovations in Gene Therapy for Sickle Cell Disease and Beta-Thalassemia
<p id="p1">Hemoglobinopathies such as sickle cell disease (SCD) and beta (β)-thalassemia are inherited disorders characterized by defective or insufficient β-globin chain production, resulting in chronic anemia, multi-organ damage, and reduced life expectancy. Affecting millions worldwide,...
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| Autores principales: | , , , , , , , , , |
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| Formato: | Capítulo de libro |
| Lenguaje: | inglés |
| Publicado: |
IntechOpen
2025
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| Materias: | |
| Acceso en línea: | https://www.intechopen.com/chapters/1226682 |
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