Perspective Chapter: Emerging Innovations in Gene Therapy for Sickle Cell Disease and Beta-Thalassemia

<p id="p1">Hemoglobinopathies such as sickle cell disease (SCD) and beta (&beta;)-thalassemia are inherited disorders characterized by defective or insufficient &beta;-globin chain production, resulting in chronic anemia, multi-organ damage, and reduced life expectancy. Affecting millions worldwide,...

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Autores principales: Thomas, Shellon, Okodaso, Henry, Kanjia, Kush, Khatu, Vaidehi, Michaud, Dervens, Singh, Kanwarjot, Jones, Kwami, Taylor, Clayton, Ikolo, Bawo Teddy, Ikolo, Felicia
Formato: Capítulo de libro
Lenguaje:inglés
Publicado: IntechOpen 2025
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Acceso en línea:https://www.intechopen.com/chapters/1226682
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