Perspective Chapter: Molecular Scissors and a Blueprint for a Cure – The Promise of Gene Editing for Sickle Cell Disease
<p>The severe hereditary condition, sickle cell disease (SCD), originates from a specific missense mutation within the gene encoding beta-globin (<i>HBB</i>). This definitive genetic alteration sets off a domino effect of pathophysiology, whose hallmark clinical manifestations include lifelong hemol...
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| Formato: | Capítulo de libro |
| Lenguaje: | inglés |
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IntechOpen
2026
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| Acceso en línea: | https://www.intechopen.com/chapters/1239632 |
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